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當雨果出生時,貝爾說:「這簡直是一個奇蹟。」
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一众新药的密集推进,让ACH治疗的市场竞争日渐激烈。对于一个患者基数有限但需终身或长期干预的罕见病市场来说,每1厘米的年生长疗效差异,从注射到口服的跨越、从日用到周剂的改进,都将成为决定未来市场格局的关键因素。